Robert Wood Johnson Medical School researcher receives fellowship for work in Canavan Disease
Scott McPhee, PhD, of Robert Wood Johnson Medical School at the University of Medicine and Dentistry of New Jersey in Camden, has been selected to receive the first Canavan Disease Clinical Research Training Fellowship which is co-sponsored by the Canavan Foundation and the American Academy of Neurology Foundation.... ...The Canavan Disease Clinical Research Training Fellowship supports research....The results of a gene therapy trial on two children with Canavan disease, a rare, fatal, inherited metabolic brain disorder, show the transfer of a therapeutic gene can be successfully and safely introduced into the brain of young patients, with some positive effects. Researchers at Jefferson Medical College, who led the 1996 trial in New Zealand - a prelude to a larger study at Jefferson in 1...